Promising Advances in Gene Therapy
More than three decades have passed since the introduction of the first human gene therapy clinical trial, yet recent advancements bring new hope. With over 40 cell and gene therapies currently approved by the US Food and Drug Administration (FDA), 2023 was notably significant as seven new therapies received approval, including the groundbreaking CRISPR-based treatment, CASGEVY®.
Although these therapies bring optimism for those suffering from complex genetic disorders, the issue of cost is a significant barrier.
